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On the HCPLive Duchenne muscular dystrophy page, resources on the topics of medical news and expert insight into DMD can be found. Content includes articles, interviews, videos, podcasts, and breaking news on the rare disease, and more.
February 28, 2022
Clinical and industry leaders share their perspectives on the importance of collaboration in developing treatments for rare diseases.
January 07, 2021
Minimal fat infiltration was observed on MR images from the SRP-9001 arm compared to participants from the natural history cohort.
August 12, 2020
The approval is based on findings from a phase 2 clinical trial.
February 29, 2020
The RareWear program is designed to bridge medical device companies to rare disease patient applicants, seeking better disease and treatment monitoring.
New research suggests proposals aimed at reducing out of pocket costs may harm minimally-funded drug developers.
December 13, 2019
The approval comes 4 months following a Complete Response Letter was submitted and successfully disputed, to Sarepta Therapeutics.
December 12, 2019
The FDA has granted marketing authorization for the GSP Neonatal Creatine Kinase-MM to aid physicians in screening newborns for Duchenne Muscular Dystrophy.